- ClinicalTrials.gov ID: NCT04729907
- Not accepting healthy volunteers
- UTSW Principal Investigator: SUSAN THERESA IANNACCONE
objective
To evaluate the long-term safety and tolerability of nusinersen administered intrathecally at higher doses to participants with SMA who previously participated in Study 203. To evaluate the long-term efficacy of nusinersen administered intrathecally at higher doses to participants with SMA who previously participated in Study 203.